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Beam Therapeutics Announced The First Patient Was Treated With BEAM-302, An Investigational In Vivo Base Editing Medicine Designed To Precisely Correct The Underlying Cause Of Severe Alpha-1 Antitrypsin Deficiency, Currently In Phase 1/2 Trial

Beam Therapeutics Announced The First Patient Was Treated With BEAM-302, An Investigational In Vivo Base Editing Medicine Designed To Precisely Correct The Underlying Cause Of Severe Alpha-1 Antitrypsin Deficiency, Currently In Phase 1/2 Trial

beam therapeutics宣佈,第一位接受BEAM-302治療的患者是嚴重的α-1抗胰蛋白酶缺乏症的病人,這是一種試驗性的原位基因編輯藥物,旨在精確糾正其潛在原因,目前處於1/2期試驗中。
Benzinga ·  06/26 18:34

Beam Therapeutics Announced The First Patient Was Treated With BEAM-302, An Investigational In Vivo Base Editing Medicine Designed To Precisely Correct The Underlying Cause Of Severe Alpha-1 Antitrypsin Deficiency, Currently In Phase 1/2 Trial

beam therapeutics宣佈,第一位接受BEAM-302治療的患者是嚴重的α-1抗胰蛋白酶缺乏症的病人,這是一種試驗性的原位基因編輯藥物,旨在精確糾正其潛在原因,目前處於1/2期試驗中。

譯文內容由第三人軟體翻譯。


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