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Ionis Pharmaceuticals Announced Topline Data From HALOS Phase 1/2A Open-label Study Of ION582 In Angelman Syndrome, ION582 Was Safe And Well Tolerated In The Study And Showed Encouraging And Consistent Benefits

Ionis Pharmaceuticals Announced Topline Data From HALOS Phase 1/2A Open-label Study Of ION582 In Angelman Syndrome, ION582 Was Safe And Well Tolerated In The Study And Showed Encouraging And Consistent Benefits

Ionis Pharmaceuticals 公佈了 HALOS 針對 ION582 的 1/2A 期開放標籤研究的主要數據,該研究顯示 ION582 安全且耐受性良好,並顯示出令人鼓舞且持續的益處
Benzinga ·  05/16 19:03
  • ION582 demonstrated consistent improvements across multiple functional domains in Angelman syndrome patients
  • ION582 was safe and well tolerated at all dose levels
  • Ionis plans to move ION582 into pivotal trial
  • Detailed ION582 data to be presented at upcoming medical meeting
  • ION582 顯示 Angelman 綜合徵患者的多個功能領域持續改善
  • ION582 在所有劑量水平下均安全且耐受性良好
  • Ionis 計劃將 ION582 轉入關鍵試驗
  • 詳細的 ION582 數據將在即將舉行的醫學會議上公佈

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