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Ionis Pharmaceuticals Announced Topline Data From HALOS Phase 1/2A Open-label Study Of ION582 In Angelman Syndrome, ION582 Was Safe And Well Tolerated In The Study And Showed Encouraging And Consistent Benefits

Ionis Pharmaceuticals Announced Topline Data From HALOS Phase 1/2A Open-label Study Of ION582 In Angelman Syndrome, ION582 Was Safe And Well Tolerated In The Study And Showed Encouraging And Consistent Benefits

Ionis Pharmaceuticals 公布了 HALOS 针对 ION582 的 1/2A 期开放标签研究的主要数据,该研究显示 ION582 安全且耐受性良好,并显示出令人鼓舞且持续的益处
Benzinga ·  05/16 19:03
  • ION582 demonstrated consistent improvements across multiple functional domains in Angelman syndrome patients
  • ION582 was safe and well tolerated at all dose levels
  • Ionis plans to move ION582 into pivotal trial
  • Detailed ION582 data to be presented at upcoming medical meeting
  • ION582 显示 Angelman 综合征患者的多个功能领域持续改善
  • ION582 在所有剂量水平下均安全且耐受性良好
  • Ionis 计划将 ION582 转入关键试验
  • 详细的 ION582 数据将在即将举行的医学会议上公布

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